This program is crafted for businesses just like yours. If you're involved in the development of gene-based therapies for ultra-rare neurological or neuromuscular disorders, this is your chance to get support for your crucial research. By applying, you open the door to funding that can help you fast-track your innovative therapies into human testing.

Here’s what you stand to gain:

• Essential funding for your research and planning activities, helping you advance towards an Investigational New Drug (IND) application.
• No immediate payback pressure, so you can focus entirely on your work without the stress of a traditional loan.
• Opportunity to be at the forefront of healthcare innovation, making a real impact by bringing life-changing therapies to those who need them most.

This program is designed to make the path to clinical trials easier. With no limits on company size or revenue, it’s accessible and aimed at propelling your promising treatments forward. Applying could be the step that transforms your ideas into reality.

Financing Offered

The financing available through this program is primarily grants. Grants are funds that you do not have to pay back, making them a fantastic opportunity for your business.

Repayment Terms and Eligible Expenses

There are no repayment terms or interest rates associated with this grant since it does not require repayment. Eligible expenses can include costs related to conducting IND-enabling studies and planning activities for the First-in-Human (FIH) clinical testing of gene therapies. Specifically, you can use the funds for research and development activities that directly support the progress of your clinical candidate.

Restrictions and Fees

You cannot use these funds for general operational costs or any unrelated expenses. Moreover, there are typically no fees associated with applying for this grant, allowing you to focus on what really matters—advancing your innovative therapies without worrying about added costs.

• Location: Available across the country.
• Sectors: Open to all sectors.
• Employees:
  • No minimum employee requirement.
  • No maximum employee limit.
• Company Revenue:
  • No minimum revenue requirement.
  • No maximum revenue limit.
• Legal Structure: All legal structures are applicable.
• Profit Structure: All profit structures are applicable.

Disqualifications: None mentioned.

Your business has a chance to receive support for important clinical studies in gene-based therapies. This funding is aimed at getting promising treatments for ultra-rare neurological and neuromuscular disorders into human testing more quickly. If you're working on a therapy with strong biological support and proof of concept, this program can help you move towards filing for Investigational New Drug (IND) status and starting clinical trials.

This program can be a game changer for your business. It provides funding to accelerate the development of innovative treatments. You can use this money for essential research and planning activities that will ultimately bring your therapy to the people who need it most. The exact amount of funding isn’t set, but the program is open to businesses of all sizes and structures across the country.

What's more, your business won’t face the pressure of immediate payback. This allows you the freedom to focus on advancing your research without the worry of repaying a loan while you navigate critical development stages. This opportunity could enhance the impact of your work and open doors to new possibilities in healthcare.